Introduction to Cancer Genetics

Cancer is a general term, describing a group of-Microsatellite instability (MIN)
different diseases. Because these diseases areMutation in both alleles necessary.
different, it is unlikely that a general cure forDNA alterations found in tumors (both malignant
cancer will evolve. Each type of cancer needs itsand benign):
own treatment program.1.Subtle alterations:
There are two common properties for all typesSmall deletions, small insertions and base-pair
of cancer:substitutions.
1. Abnormal proliferation (so called neoplasia, that2.Chromosome number change (aneuploidy):
results in a neoplasm structure)Gain and loss of chromosomes (Which may result
2. Invasive ability. Property that separates benignin that both chromosomes are from the same
tumors from cancer.parent. A loss of one chromosome often leads to
Cancer cells invade other regions by travellingthe duplication of the remaining chromosome).
through the circulatory system or lymphaticA typical phenomena is loss of heterozygosity
system. This process is called metastasis, in which(LOH), which can lead to the inactivation of genes
disease is spread from one organ to another(these genes may be suppressor genes, that
non-adjacent organ.protect the cell from cancer)
Cancers can be classified according to cell type.3. Chromosome translocation:
1.Leukemia and LymphomaCan be either:
2.Carcinoma1.Balanced (even exchange of material)
3.Sarcoma2.Unbalanced (unequal exchange of material).
4.MelanomaResults in extra or missing genes.
5.Retinoblastoma, Neuroblastoma, GlioblastomaTranslocation leads to Malignity:
(1: blood-borne cancers, 2-5: solid tumors)- Transcription factor genes are moved (to the
Cancer is a genetic disease and can also be seenvicinity of highly active promotor/enhancer
as a disturbance in the cell cycle regulationelements) and thus become over expressed.
system. You can inherit a predisposition for- Tyrosine kinase genes are fused with normal
cancer, but for the disease to break out additionalgenes and translation results in a chimeric protein
somatic mutations are required. These mutationswith oncogenic properties = fusion protein (growth
arise from:factor receptor or intracellular signal transducers).
1. Environmental mutagens (physical or chemicalChromosome translocation in Leukemia and
agents that change DNA)Lymphoma:
2. Imperfections during DNA copying and repairTranslocations are specific (not random).
(so called spontaneous mutations).- Transcription factor translocation:
There are two ways to categorize mutatedA. Acute Lymphoblastic Leukemia and
genes based on function:Non-Hodgkin Lymphoma (e.g. MYC)
1.Function in a cancer cellB. Acute Myeloid Leukemia (e.g. AML1-CBF²
- Genes that have been activated or overcomplex)
expressed = oncogenes (one mutated allele isC. Acute Mixed-Lineage Leukemia
enough)- Tyrosine kinase translocation
- Genes that have been inactivated:A. Chronic Myeloid Leukemia (ABL fusion gene)
1.Tumor suppressor genes.B. Acute Lymphoblastic Leukemia (ABL fusion
Both alleles need to be mutated. E.g. RB1 and p53gene)
2. DNA-mismatch repair genesThe Philadelphia chromosome is used as a marker
Both alleles need to be mutated.in prognosis and in follow- up of treatment.
2.Function in normal cell:4. Amplification:
- Genes that directly control proliferationDefined as over 6 copies of a DNA region (called
(controlling cell birth rate or death rate) =the amplicon).
GatekeepersThese regions most frequently code for:
- Genes that control the rate of mutation =1.Transcriptional factors (MYC-family, e.g. MYCN
Caretakersamplification seen in neuroblastoma)
Mutation in some genes always leads to the same2.Signal transduction molecules (Ras-family)
type of cancer, independent of what kind of3.Growth factors (EGF, FGF), Growth factor
mutation or where it has arisen (e.g.WT1).receptors (EGFR, FGFR)
Mutations in other genes result in many different4.Regulators of the cell cycle.
forms of cancer (e.g. p53).Over expression of these genes gives cancer a
Neoplasms have genetic instability. It is not clear ifgrowth advantage.
the instability is the reason for tumor formation orThe amplification can be outside the chromosome
just a consequence. This instability can be divided(double minute chromatin bodies) or within the
into two major groups:chromosome.
1.Instability at the chromosomal level (CIN)Amplifications can be used in prognosis and
Mutation in one allele enough. Hypomethylationtargeted gene therapy.
increases instability.5. Exogenous sequences:
2.Instability at the nucleotide level: Faulty DNAE.g. tumor viruses which activate either human
repair pathwaysgenes or viral genes that lead to the accumulation
-Nucleotide Excision Repair Instability (NIN)of mutations.